Femme et Homme
- | Pays :
- Netherlands
- Sweden
- United Kingdom
- Les 10 autres...
- | Organes : -
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Extrait
The objectives of this program are: to further characterize the natural progression of MPS VI disease; to generate and disseminate information on the care and management of MPS VI patients to clinical and medical professionals; to provide a resource to physicians and patients by providing information for optimizing patient care based on aggregate data; to characterize the clinical response to long-term Naglazyme® (galsulfase) treatment; to further characterize the long-term safety of Naglazyme® treatment.
Critère d'inclusion
- Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome)